Ribozyme and omics

Anti-cancer development based on RNA Platform technology Core competence to meet diverse unmet medical needs


Retinitis Pigmentosa (RP)

Medical unmet needs
  • High rate of blindness

    The most common inherited retinal diseases, one of the main causes of blindness

    Gradual loss of photoreceptor leading to retina regression/atrophy

    Incidence rate: 1/3,500~4,000 (US/EU)

  • Lack of effective therapies

    Only possible to delay visual loss and to restore partial visual acuity

    Autosomal recessive, dominant, X-linked RP

    Clinical researches on gene therapies and stem cell therapies

  • In need of new therapies

    Almost no clinical trials on Autosomal dominant (AD RP)

    AD RP: In need of WT gene expression as well as antimutagenic effect